Clinical Trials Research on Rare Diseases: N
- N-acetylglutamate Synthetase Deficiency 1 study
- Nail Patella Syndrome 1 study
- Narcolepsy 36 studies
- Nasopharyngeal Carcinoma 366 studies
- Necrotizing Enterocolitis 66 studies
- Necrotizing Fasciitis 6 studies
- Neisseria Meningitidis Infection 85 studies
- Nelson Syndrome 2 studies
- Neonatal Herpes 5 studies
- Neonatal Hypothyroidism 1 study
- Neonatal Meningitis 1 study
- Neonatal Ovarian Cyst 1 study
- Neonatal Stroke 5 studies
- Neonatal Systemic Lupus Erythematosus 4 studies
- Nephrocalcinosis 6 studies
- Nephrogenic Diabetes Insipidus 4 studies
- Nephrogenic Systemic Fibrosis 16 studies
- Nephropathic Cystinosis 59 studies
- Nephrosclerosis 2 studies
- Nerve Sheath Neoplasm 15 studies
- Netherton Syndrome 4 studies
- Neuroacanthocytosis 1 study
- Neuroblastoma 393 studies
- Neuroepithelioma 3032 studies
- Neurofibroma 92 studies
- Neurofibromatosis 76 studies
- Neurofibromatosis Type 1 63 studies
- Neurofibromatosis Type 2 18 studies
- Neurofibrosarcoma 52 studies
- Neurogenic Diabetes Insipidus 20 studies
- Neuroleptic Malignant Syndrome 7 studies
- Neuromyelitis Optica Spectrum Disorder 4 studies
- Neuronal Ceroid Lipofuscinoses 12 studies
- Neuropathy Hereditary Sensory and Autonomic Type 1 1 study
- Neurosyphilis 3 studies
- Neurotoxicity Syndromes 411 studies
- Neutral Lipid Storage Disease With Myopathy 1 study
- Nevoid Basal Cell Carcinoma Syndrome 13 studies
- New Daily-persistent Headache 1 study
- Niemann-Pick Disease 19 studies
- Niemann-Pick Disease Type B 1 study
- Niemann-Pick Disease Type C1 16 studies
- Nodular Melanoma 4 studies
- Nodular Regenerative Hyperplasia 5 studies
- Non 24 Hour Sleep Wake Disorder 5 studies
- Non-Hodgkin Lymphoma, Childhood 10 studies
- Nonalcoholic Steatohepatitis 223 studies
- Nonbullous Congenital Ichthyosiform Erythroderma 4 studies
- Nondystrophic Myotonia 2 studies
- Nonseminomatous Germ Cell Tumor 24 studies
- Noonan Syndrome 10 studies
- Noonan Syndrome 1 10 studies
- Norrie Disease 2 studies
- Norum Disease 2 studies
- Notalgia Paresthetica 1 study