A Study of the Safety and Pharmacokinetics of rhGAA in Siblings With Glycogen Storage Disease Type II
Condition(s): Glycogen Storage Disease Type II; Pompe Disease; Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: July 6, 2009Completed
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Condition(s): Glycogen Storage Disease Type II; Pompe Disease; Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: July 6, 2009Completed
Condition(s): Glycogen Storage Disease Type II; Pompe Disease; Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: March 14, 2011Completed
Condition(s): Pompe Disease; Glycogen Storage Disease Type II; Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: August 4, 2009Completed
Condition(s): Pompe Disease (Late-Onset); Glycogen Storage Disease Type II (GSD-II); Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: July 7, 2009Completed
Condition(s): Pompe Disease (Late-onset); Glycogen Storage Disease Type II (GSD-II); Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: June 24, 2010Completed
Condition(s): Pompe Disease (Late-Onset); Glycogen Storage Disease Type II (GSD-II); Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: July 7, 2009Completed
Condition(s): Pompe Disease (Infantile-Onset); Glycogen Storage Disease Type II (GSD II); Glycogenosis 2; Acid Maltase Deficiency Last Updated: May 2, 2013Recruiting
Condition(s): Pompe Disease (Late-Onset); Glycogen Storage Disease Type II (GSD II); Glycogenesis 2 Acid Maltase Deficiency Last Updated: July 7, 2009Completed
Condition(s): Pompe Disease (Late-Onset); Glycogen Storage Disease Type II (GSD II); Glycogenesis 2 Acid Maltase Deficiency Last Updated: April 4, 2013Recruiting
Condition(s): Pompe Disease Late-Onset; Glycogen Storage Disease Type II GSD II Last Updated: July 7, 2009Completed
Condition(s): Glycogen Storage Disease Type II (GSD-II); Pompe Disease (Late-onset); Glycogenesis 2 Acid Maltase Deficiency Last Updated: April 4, 2013Recruiting
Condition(s): Glycogen Storage Disease Type II; Pompe Disease Last Updated: January 30, 2013Recruiting
Condition(s): Glycogen Storage Disease Type II; Glycogenosis 2 Last Updated: April 12, 2012Approved for marketing
Condition(s): Glycogen Storage Disease Type II; Glycogenosis 2 Last Updated: October 14, 2008Completed
Condition(s): Glycogen Storage Disease Type II (GSD-II); Pompe Disease (Late-onset); Acid Maltase Deficiency Disease; Glycogenosis 2 Last Updated: October 25, 2010Approved for marketing
Condition(s): Pompe Disease; Glycogen Storage Disease Type II (GSD-II); Glycogenesis 2 Acid Maltase Deficiency Last Updated: March 18, 2013Recruiting
Condition(s): Pompe Disease; Glycogen Storage Disease Type II (GSD-II); Glycogenesis 2 Acid Maltase Deficiency Last Updated: March 23, 2011Completed
Condition(s): Pompe Disease; Glycogen Storage Disease Type II (GSD-II); Acid Maltase Deficiency Disease Last Updated: March 14, 2013Recruiting
Condition(s): Pompe Disease Infantile-Onset; Glycogen Storage Disease Type II Last Updated: July 7, 2009Completed
Condition(s): Pompe Disease (Late-Onset); Glycogen Storage Disease Type II (GSD-II); Glycogenesis Type II; Acid Maltase Deficiency (AMD) Last Updated: January 10, 2012Completed