30 Clinical Trials for: SEARCH[STUDY] Sanfilippo Syndrome, Page 1 of 2

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Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders

Condition(s): Hurler Syndrome (MPS I); Hurler-Scheie Syndrome With Early Neurologic Involvement and/or Sensitization to Enzyme Replacement Therapy (ERT); Hunter Syndrome (MPS II); Sanfilippo Syndrome (MPS III); Krabbe Disease (Globoid Leukodystrophy); Metachromatic Leukodystrophy (MLD); Adrenoleukodystrophy (ALD and AMN); Sandhoff Disease; Tay Sachs Disease; Pelizaeus Merzbacher (PMD); Niemann-Pick Disease; Alpha-mannosidosis Last Updated: April 5, 2016Active, not recruiting